Health and quality of life after sibling stem cell transplant for sickle cell disease
Part of Blood & lymphatic, Genetic & congenital clinical trials.
This study compares the health status and quality of life of people with sickle cell disease who had a stem cell transplant from a brother or sister, between 2000 and 2012, with people who did not have the transplant. The goal is to understand how the transplant affects long-term well-being.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You must have sickle cell anemia (SS or S-beta0 type).
- You had a stem cell transplant from a brother or sister (or sibling cord blood) between 2000 and 2012.
- Before transplant, you received a specific conditioning regimen (busulfan, cyclophosphamide, and anti-thymocyte globulin).
- If you are under 18, your parents must sign a consent form. If you are 18 or older, you must sign.
- You must be covered by French social security (health insurance).
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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