Health and quality of life after sibling stem cell transplant for sickle cell disease
Part of Blood & lymphatic, Genetic & congenital clinical trials.
This study looks at how patients with sickle cell disease who had a stem cell transplant from a sibling are doing now, compared to patients who didn't have a transplant. It focuses on health status and quality of life over the long term.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You have sickle cell anemia (type SS or S-beta-zero).
- You had a stem cell transplant from a sibling (or their cord blood) between 2000 and 2012.
- You received a specific pre-transplant treatment (busulfan, cyclophosphamide, and anti-thymocyte globulin).
- You are willing and able to give informed consent (or have a parent/guardian do so if under 18).
- You are covered by French social security.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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