Gene therapy for neurofibromatosis type 2 (NF2)
Part of Brain & nervous system, Cancer, Genetic & congenital clinical trials.
This trial tests a gene therapy called ST002 for people with NF2-related tumors that cannot be treated with standard therapies or have not responded to them. The treatment is injected directly into a tumor, and the goal is to see if it can shrink or control the tumor.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You are 16 years or older
- You have a confirmed NF2 gene mutation or loss of Merlin protein, and standard treatments have failed or are not available
- You have at least one tumor just under the skin that can be measured and injected
- Your blood counts, liver, kidney, and clotting function are within acceptable ranges
- You are willing to use birth control if you are a woman of childbearing age
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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