Observational study of amyloidosis and TTR gene carriers
Part of Brain & nervous system, Genetic & congenital, Heart & circulation, Hormones & metabolism clinical trials.
This study is observing people with amyloidosis or those who carry a specific gene mutation (transthyretin) to learn more about the condition. It does not test any new treatment, but may help researchers understand how the disease affects people.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You have been diagnosed with amyloidosis, or you carry a mutation in the transthyretin gene (even if you have no symptoms).
- You were at least 18 years old when you were diagnosed.
- You agree to sign a consent form to take part in the study.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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