Clin2
NCT07024394Likely a fitNot yet recruiting

Long-term safety of FCN-159 in children with NF1

Neurofibromatosis 1Plexiform NeurofibromaNF1

Treatments studied

Part of Brain & nervous system, Cancer, Genetic & congenital clinical trials.

This study follows up with children who took part in an earlier trial of FCN-159, a drug for a condition called Neurofibromatosis Type 1 (NF1). It aims to see how safe and effective the drug is over a longer period.

Summary written for real people, not researchers, by Clin2.

Phase
Phase 1/Phase 2
Enrollment
65 people
Ages
2 years to 20 years
Study type
Interventional

Who can take part

  • You took part in the earlier FCN-159-002 study for children.
  • You are willing to join this longer follow-up study.
  • You can understand and sign a consent form explaining the study.
  • You do not have any other health issues that would make it unsafe to continue.
  • You are able to come to all scheduled visits.

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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