Clin2
NCT07264166Possibly a fitEnrolling by invitation

Gene therapy trial for cerebral palsy and HIE

Hypoxic Brain DamageHypoxic Ischaemic Encephalopathy (HIE)Hypoxic Ischaemic Encephalopathy Due to Cardiac ArrestHypoxic Ischemic Encephalopathy of NewbornCerebral PalsyCerebral Palsy (CP)Cerebral Palsy Hemiparetic Cerebral Palsy Spasticity Gait Disorders, Neurologic Postural Balance ImpairmentCerebral Palsy Quadriplegic

Part of Brain & nervous system, Heart & circulation, Mental health clinical trials.

This trial tests a gene therapy given as a nose spray for people with cerebral palsy or HIE. It aims to see if the treatment is safe and helps improve movement over two years.

Summary written for real people, not researchers, by Clin2.

Phase
N/A
Enrollment
25 people
Ages
2 years to 65 years
Study type
Observational

Who can take part

  • You must be between 2 and 65 years old.
  • You must have a doctor's diagnosis of HIE (brain injury from lack of oxygen at birth), confirmed by medical records or MRI.
  • Your health must be stable for at least 6 months (no major surgeries or hospital stays related to HIE).
  • You must have a moderate level of movement problems (GMFM score between 40% and 70%).
  • You must have already received or are now getting the study gene therapy nose spray at a participating clinic.
  • Your parent or guardian must agree to take part in this registry and let your data be used.

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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