Stem cell collection study for sickle cell disease patients
Part of Blood & lymphatic, Genetic & congenital clinical trials.
This trial tests a high-dose medicine to collect stem cells from young adults with sickle cell disease. It aims to prepare for a transplant that could potentially cure the condition.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You are between 18 and 25 years old
- You have sickle cell disease and a doctor says you may need a stem cell transplant
- You need to be in fairly good health, with good blood counts and no major organ problems
- You can have a transfusion to lower your sickle hemoglobin below 30% before starting
- You are not pregnant, not breastfeeding, and agree to use two forms of birth control
- You can stop taking hydroxyurea for at least 30 days before the study
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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