Piclidenoson for Lowe syndrome
Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism, Kidney & urinary, Women’s health & pregnancy clinical trials.
This trial tests an experimental medicine called piclidenoson for people with Lowe syndrome, a rare condition that affects the kidneys, eyes, and brain. The study aims to see if the medicine is safe and effective in improving kidney function or other symptoms.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You are male and 18 years or older.
- You have a confirmed diagnosis of Lowe syndrome through genetic testing.
- Your kidney function is at least 40% of normal (measured by a standard test).
- You are willing to use condoms during the study and for 1 month after the last dose, and you will not donate sperm.
- You can attend study visits and follow the study plan, and you can give written consent (or have a legal guardian do it).
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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