Clin2
NCT07601425Likely a fitRecruiting

ATV-1601 Treatment for Hereditary Hemorrhagic Telangiectasia

Hereditary Hemorrhagic Telangiectasia (HHT)Osler Weber Rendu Disease

Part of Blood & lymphatic, Genetic & congenital, Heart & circulation clinical trials.

This trial tests a new drug called ATV-1601 in people with HHT, a genetic condition that causes abnormal bleeding and blood vessel problems. The drug aims to reduce bleeding and anemia caused by HHT.

Summary written for real people, not researchers, by Clin2.

Phase
Phase 1/Phase 2
Enrollment
100 people
Ages
18 years and older
Study type
Interventional

Who can take part

  • You have a confirmed diagnosis of HHT (hereditary hemorrhagic telangiectasia), a genetic bleeding disorder
  • Your HHT is moderate to severe with a specific symptom score of 4 or higher
  • You have anemia or needed at least one blood transfusion in the past 6 months
  • Your blood, kidney, and liver function tests are adequate for the study
  • You are not pregnant, not breastfeeding, and able to use effective birth control during and after the study
  • You have not taken an AKT inhibitor before (a type of cancer drug)

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

Similar studies

Other trials that look related to this one.

NCT07667413Not yet recruiting· Phase 1
Test of a new nose spray for nosebleeds in HHT

This trial tests a new nose spray (TOR-582) to reduce nosebleeds in people with HHT. If you have moderate nosebleeds, this treatment might help decrease how often and how long they last.

New York, New York
NCT07445347Enrolling by invitation
Bevacizumab for severe HHT liver issues with high heart output

This study looks at how well the drug Bevacizumab works and how safe it is for people with HHT who have severe liver problems that cause their heart to pump too much blood. It aims to help doctors understand if this treatment can help manage these serious symptoms.

Poitiers
NCT07623525Recruiting· Phase 1/Phase 2
DIAG723 study for hereditary hemorrhagic telangiectasia

This study tests a new drug called DIAG723 in adults with hereditary hemorrhagic telangiectasia (HHT), a genetic condition that causes abnormal blood vessels and bleeding. Depending on which part of the study you qualify for, the drug may help reduce nosebleeds, improve anemia, or help with lung blood vessel problems caused by HHT.

Camperdown, New South Wales
NCT04976036Recruiting· Phase 2
Nintedanib to reduce nosebleeds in adults with HHT

This trial tests whether nintedanib can reduce how often and how severe nosebleeds are in adults with hereditary hemorrhagic telangiectasia (HHT). It may help by calming blood-vessel problems that cause bleeding.

Bron
NCT07743671Not yet recruiting· Phase 3
Engasertib for frequent nosebleeds from HHT

This trial tests an experimental pill, engasertib, to reduce frequent nosebleeds in adults with a rare blood vessel condition called hereditary hemorrhagic telangiectasia (HHT). Participation may help if you have moderate to severe nosebleeds and need iron or blood transfusions.

NCT07101575Not yet recruiting
Heart checkup for people with HHT

This study uses an echocardiogram (a heart ultrasound) to look for possible heart problems in people with hereditary hemorrhagic telangiectasia (HHT). It will help doctors understand how HHT affects the heart.

Hear when a new Hereditary Hemorrhagic Telangiectasia (HHT) trial opens

We’ll email you when one opens — at most once a week, no account needed, unsubscribe anytime.