Study of KRRO-121 in healthy adults and people with urea cycle disorder
Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism clinical trials.
This study tests an investigational drug called KRRO-121. It is first tested in healthy volunteers to check safety, and then in patients with urea cycle disorder (a condition where the body can't remove ammonia properly) to see if it helps.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You are between 18 and 65 years old.
- You are generally healthy (for the healthy volunteer part) or have urea cycle disorder (for the patient part).
- You are willing to use reliable birth control if you or your partner can become pregnant.
- You can give informed consent and follow the study rules.
- You have not used an investigational drug or device in the last 3 months.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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