Study of daily injections for Friedreich's ataxia
Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism clinical trials.
This study tests an investigational drug given as a daily injection to see if it can improve walking and balance in people with Friedreich's ataxia.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You must have a genetic test showing two abnormal copies of the FXN gene.
- You must be able to walk 25 feet in under 3 minutes (with or without a walking aid).
- You must have moderate but not severe balance and coordination problems.
- You (or a caregiver) must be able to give daily injections under the skin.
- You must not be pregnant, breastfeeding, or planning pregnancy during the study.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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