Study of GV101 for Friedreich's ataxia
Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism clinical trials.
This study tests a new medicine called GV101 to see if it can help people with Friedreich's ataxia, a condition that affects movement and balance. The trial will check if GV101 is safe and if it improves symptoms.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You are between 16 and 40 years old.
- You have a confirmed diagnosis of Friedreich's ataxia with the typical genetic change (homozygous GAA repeat expansion).
- Your movement and coordination scores must be within a certain range (mFARS 20-80).
- You can walk with or without a walker or cane, and you can sit upright.
- You have a heart test (troponin) above a specific level, which may indicate early heart stress.
- You are not taking certain medications or have not had gene therapy for Friedreich's ataxia.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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