Rare blood disease network for better care
Part of Blood & lymphatic, Genetic & congenital, Hormones & metabolism, Skin clinical trials.
This study creates a national network to collect health information and samples from people with certain rare blood diseases. The goal is to improve treatment and understand these conditions better.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You have been diagnosed with a rare blood disease such as Fanconi anemia, dyskeratosis congenita, telomere biology disorders, congenital neutropenia, primary immune regulatory disorders, congenital amegakaryocytic thrombocytopenia, or acquired aplastic anemia (with or without PNH).
- You or your legal guardian sign a consent form agreeing to join.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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