Study of a rare muscle condition linked to Paget bone disease
Part of Bones, joints & muscles, Brain & nervous system, Hormones & metabolism, Mental health clinical trials.
This study looks at people and families with a rare muscle weakness condition that can be linked with Paget disease of the bone (and sometimes frontotemporal dementia). It aims to better describe how these conditions appear and relate, which can help future research and care.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You (or your affected family member) are an adult age 18 or older
- You can understand and agree to participate (give consent)
- You have a muscle condition such as inclusion body myopathy or certain muscular dystrophies
- You also have a bone condition such as Paget disease of bone (or similar listed bone problems)
- You can participate either as the affected person or as an adult family member/spouse
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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