Osilodrostat study for children with Cushing’s syndrome
Part of Brain & nervous system, Hormones & metabolism clinical trials.
This Phase 2 study tests how osilodrostat works in children and teens with Cushing’s syndrome—what the drug does in the body, how it affects hormones, and how safely it’s tolerated. It may help families who cannot have immediate surgery or whose surgery has already failed or is still pending.
Summary written for real people, not researchers, by Clin2.
Who can take part
- Be age 2 up to under 18, and have Cushing’s syndrome caused by your own body
- Have had surgery that failed, or be waiting for surgery, or surgery is not an option right away (waiting can be under 12 weeks)
- Weigh more than 10 kg
- Have confirmed Cushing’s diagnosis with blood, urine, and/or hormone testing done as specified by the study
- Be able to swallow study tablets whole (or take capsule contents mixed with water)
- Have a parent/guardian who can give consent (and the child can assent if required)
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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