Clin2
NCT05650229Possibly a fitRecruiting

Study of KL1333 for adult mitochondrial disease fatigue and weakness

Primary Mitochondrial Disease

Part of Bones, joints & muscles, Brain & nervous system, Hormones & metabolism clinical trials.

This Phase 2 trial studies whether KL1333 improves chronic fatigue and muscle weakness in adults with a confirmed mitochondrial genetic disease. You may be eligible if you have persistent fatigue for at least 3 months and signs of muscle involvement, and can safely follow study requirements.

Summary written for real people, not researchers, by Clin2.

Phase
Phase 2
Enrollment
180 people
Ages
18 years and older
Study type
Interventional

Who can take part

  • You are age 18 or older with a confirmed mitochondrial disease linked to a known gene or mtDNA deletion
  • Your mitochondrial disease affects multiple body systems (not mainly brain/nerve degeneration conditions like Leigh or LHON)
  • You’ve had mitochondrial fatigue for at least 3 months and your fatigue score is at a moderate level or higher
  • You have signs of muscle involvement or limited exercise tolerance on the study’s strength/mobility checks
  • You can safely do the 30-second sit-to-stand test within the allowed repetition range, and you’re generally medically stable
  • You can follow key medication and lifestyle rules, including stable diet and holding certain supplements; and certain pregnancy protections if applicable

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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