Clin2
NCT05735184Possibly a fitRecruiting

Ziftomenib with AML medicines for NPM1- or KMT2A-mutated leukemia

Acute Myeloid LeukemiaMixed Lineage Leukemia Gene MutationRefractory AMLAML With Mutated NPM1Acute Myeloid Leukemia RecurrentAcute Myeloid Leukemia, in RelapseNPM1 MutationKMT2Ar

Treatments studied

Part of Blood & lymphatic, Cancer clinical trials.

This Phase 1 trial tests how safe and tolerable ziftomenib is when combined with standard AML medicines (like venetoclax and azacitidine, and other chemo options) in people with AML. It’s for AML patients who have specific genetic changes (NPM1 mutation or KMT2A rearrangement) and helps doctors find the best, safest dose plan.

Summary written for real people, not researchers, by Clin2.

Phase
Phase 1
Enrollment
420 people
Ages
18 years and older
Study type
Interventional

Who can take part

  • You have AML that is newly diagnosed or has come back (relapsed) or not responded (refractory).
  • Your leukemia test shows either an NPM1 mutation or a KMT2A rearrangement.
  • Your overall health ability to function day-to-day is ECOG 0, 1, or 2 (meaning you’re able to do self-care and light activity).
  • Your heart, kidney, and liver tests meet the study’s required levels.
  • You cannot be pregnant or breastfeeding, and you must follow strict birth-control rules during the study and for 180 days after the last dose (or special extra rules if receiving quizartinib).

View the official record on ClinicalTrials.gov

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Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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