Long-term study of JNT-517 for people with PKU
Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism clinical trials.
This study tests a new medicine called JNT-517 for people with phenylketonuria (PKU) over a long period. It aims to see if the drug can help manage PKU safely and effectively.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You have been diagnosed with phenylketonuria (PKU).
- You are 4 years old or older.
- You have not taken pegvaliase (a PKU drug) in the last 4 weeks.
- You have not taken sepiapterin (another PKU drug) in the last 2 weeks.
- You are willing to follow a stable diet and come for regular check-ups.
- You weigh at least 12.5 kg (about 28 pounds).
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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