Study of an experimental pill for adults with PKU
Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism clinical trials.
This trial tests an experimental medication taken as a pill to see if it can help people with PKU manage their condition. The study will check if the pill is safe and how it affects blood phenylalanine levels.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You are between 18 and 75 years old
- You have been diagnosed with PKU (phenylketonuria)
- You are willing to keep your diet and protein intake the same during the study
- If you are in certain study groups, you must be willing to stop taking some PKU medications before starting the study pill
- Depending on the group, you may need to have a certain blood phenylalanine level or meet other treatment requirements
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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