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NCT07318909Possibly a fitNot yet recruiting

Testing GS1168 injection for adults with PKU

Phenylketonuria (PKU)

Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism clinical trials.

This study tests a new injection called GS1168 for adults with phenylketonuria (PKU) whose current treatments are not working well. The goal is to see if it can help control their PKU better.

Summary written for real people, not researchers, by Clin2.

Phase
Early Phase 1
Enrollment
9 people
Ages
18 years to 55 years
Study type
Interventional

Who can take part

  • You are between 18 and 55 years old.
  • You have PKU caused by a specific gene change (PAH) and current treatments are not working well enough.
  • You have tried or cannot take certain PKU medications (Kuvan or Palynziq) and have been off them for at least 28 days.
  • You are willing to keep your protein intake from food steady during the study.
  • You agree to avoid alcohol for a long period (from 30 days before treatment to 52 weeks after).

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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Angers

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