Inhaled gene therapy trial for cystic fibrosis patients aged 12+
Part of Digestive system, Genetic & congenital, Lungs & breathing clinical trials.
This trial tests a new inhaled medicine (BMD003) that delivers CFTR mRNA to help correct the genetic defect causing cystic fibrosis. It is for patients who are 12 years or older, have stable CF, and meet certain lung function and weight criteria.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You must be 12 years old or older.
- You must have a confirmed diagnosis of cystic fibrosis and be in stable health.
- You must weigh at least 40 kg if 18 or older, or at least 30 kg if under 18.
- Your lung function (FEV1) must be at least 40% of normal, and your oxygen level at rest must be 92% or higher.
- You must not smoke or have smoked in the last 2 years.
- You must be willing to follow all study procedures and attend follow-up visits.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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