Clinical trials
Paroxysmal Nocturnal Hemoglobinuria clinical trials
Below are recruiting paroxysmal nocturnal hemoglobinuria clinical trials, each written for real people, not researchers. We’re tracking 29 recruiting studies, each written for real people, not researchers, below.
Recruiting studies
- NCT06524726Recruiting
PNH registry for people with confirmed PNH
This is a long-term registry study for people with a confirmed diagnosis of paroxysmal nocturnal hemoglobinuria (PNH). It simply collects information over time to better understand the condition and how it's managed. There is no experimental treatment involved.
Altamonte Springs, FloridaAges Any age - NCT06931691Recruiting
Study of Iptacopan for adults with PNH in China
This study looks at how well iptacopan works for people with PNH (a condition where red blood cells break down too quickly). It is for adults who have never used certain treatments or who have been on other similar medicines.
Hefei, AnhuiAges 18–80 - NCT06932471RecruitingPhase 3
Study of a new drug for PNH patients with anemia despite current treatment
This trial tests a new pill (MY008211A) for people with paroxysmal nocturnal hemoglobinuria (PNH) who still have low red blood cell counts (anemia) even after taking anti-C5 antibody therapy. The goal is to see if this new drug can raise hemoglobin levels and improve energy.
Beijing, Beijing MunicipalityAges 18–75 - NCT07152288RecruitingPhase 1
Study of HSK39297 in people with liver problems
This trial tests how a new drug, HSK39297, works in people with mild to moderate liver impairment (Child-Pugh A or B). It compares them to healthy volunteers to see how the liver affects the drug's safety and how the body processes it.
BeijingAges 18–70 - NCT07462780RecruitingPhase 1
Testing CMS-D017 in Healthy Volunteers
This trial tests a new investigational drug called CMS-D017 in healthy volunteers. Researchers will give single and multiple doses to see how the body processes it and if it's safe. You could help find an important new treatment.
BeijingAges 18–55
Hear when a new Paroxysmal Nocturnal Hemoglobinuria trial opens
We’ll email you when one opens — at most once a week, no account needed, unsubscribe anytime.
Common questions
- Are there clinical trials for paroxysmal nocturnal hemoglobinuria?
- Yes. Clin2 currently lists 29 recruiting paroxysmal nocturnal hemoglobinuria studies from the U.S. registry, each rewritten for real people, not researchers, so you can see what it’s testing and who it’s for.
- How do I know if I qualify for a paroxysmal nocturnal hemoglobinuria trial?
- Each study lists its eligibility criteria — rules about age, diagnosis, and prior treatments. On every Clin2 trial page we explain these in words written for real people and offer a short, optional pre-screen for a fit read. The study team makes the final decision.
- Does it cost anything to join a paroxysmal nocturnal hemoglobinuria trial?
- Using Clin2 is always free. Many trials cover the cost of the study treatment and related visits; some reimburse travel. The study team explains exactly what’s covered before you decide.
Related conditions
Clin2 helps you find and understand clinical trials and does not provide medical advice. Study data comes from ClinicalTrials.gov. Talk with your doctor about whether a specific trial is right for you.