Clin2
NCT01852370Possibly a fitEnrolling by invitation

Lung and bone marrow transplant plan for immune system disorders

Severe Combined Immunodeficiency (SCID)Immunodeficiency With Predominant T-cell Defect, UnspecifiedSevere Chronic NeutropeniaChronic Granulomatous Disease (CGD)Hyper IgE SyndromesHyper IgM DeficienciesWiskott-Aldrich SyndromeMendelian Susceptibility to Mycobacterial Disease

Part of Blood & lymphatic, Genetic & congenital, Hormones & metabolism, Immune system & allergy clinical trials.

This early-phase study tests a step-by-step transplant approach: first replacing the lungs, then doing a bone marrow (stem cell) transplant to treat certain immune deficiency diseases. It may help people whose immune problem has led to severe, end-stage lung disease.

Summary written for real people, not researchers, by Clin2.

Phase
Phase 1/Phase 2
Enrollment
16 people
Ages
5 years to 45 years
Study type
Interventional

Who can take part

  • You (or your parent/guardian) must be able and willing to understand the study and sign consent forms.
  • Age 5 to 45 years at the time you sign consent.
  • You must have a known immune system disorder where a bone marrow transplant is medically recommended.
  • Your lung disease must be advanced enough that the lung transplant team says you are a candidate for a lung transplant in both lungs.
  • Your heart, liver, and kidney results must meet the study’s thresholds (kidney function, liver enzymes, bilirubin, and heart pumping strength).

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

Similar studies

Other trials that look related to this one.

NCT07284641Recruiting· Phase 2
Stem cell transplant for immune disorders

This trial tests a stem cell transplant to treat common variable immunodeficiency (CVID) and other immune problems. It aims to replace a faulty immune system with a healthy one from a donor.

Pittsburgh, Pennsylvania
NCT03500731Recruiting· Phase 1/Phase 2
Lung and bone marrow transplant for lung and blood failure

This Phase 1/2 study tests a special lung-and-bone-marrow transplant approach for people with severe lung disease and bone marrow failure (low blood counts). The goal is to see if the treatment is safe and whether it can improve outcomes when standard long-term immune-suppressing medicines are a poor fit.

Pittsburgh, Pennsylvania
NCT01962415Recruiting· Phase 2
Reduced-intensity stem cell transplant for non-cancer disorders

This trial tests whether a gentler (reduced-intensity) conditioning treatment before a stem cell transplant works for non-cancer diseases. It uses specific donor stem cell matches and checks heart, lung, liver, and kidney function to help lower transplant stress while still aiming for benefit.

Pittsburgh, Pennsylvania
NCT04528355Recruiting
Study of hospital data after stem cell transplant for non-cancer illness

This study collects medical information from people with certain non-cancer conditions who receive a stem cell transplant. It may help doctors better understand transplant outcomes and care, since the study focuses on data collection rather than adding new treatment.

Pittsburgh, Pennsylvania
NCT04339777Recruiting· Phase 2
Bone marrow transplant for inherited immune system disorders

This trial studies how well a donor bone marrow (stem cell) transplant works for people with inherited immune system problems (called immune deficiencies). It’s for patients who haven’t improved with usual treatment or don’t have another good option.

Bethesda, Maryland
NCT02579967Recruiting· Phase 2
Stem cell transplant for primary immune system disorders

This study tests whether an allogeneic stem cell (bone marrow) transplant can correct an inherited immune problem in people with severe primary immunodeficiencies. It may help reduce life-threatening infections and improve quality of life, depending on your overall health and donor match.

Bethesda, Maryland

Hear when a new Severe Combined Immunodeficiency (SCID) trial opens

We’ll email you when one opens — at most once a week, no account needed, unsubscribe anytime.