Stem cell transplant for immune disorders
Part of Blood & lymphatic, Bones, joints & muscles, Digestive system, Genetic & congenital, Heart & circulation, Hormones & metabolism, Immune system & allergy clinical trials.
This trial tests a stem cell transplant to treat common variable immunodeficiency (CVID) and other immune problems. It aims to replace a faulty immune system with a healthy one from a donor.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You must be between 5 and 40 years old.
- You have been diagnosed with CVID or another immune regulation disorder.
- Two specific treatments (mycophenolate mofetil and a drug like rituximab) have not worked for you.
- Your heart, lungs, kidneys, and liver must be working well enough for the transplant.
- You must agree to use birth control for up to 12 months after the transplant.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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