Clin2
NCT04558736Possibly a fitRecruiting

Haploidentical transplant for severe aplastic anemia in children

Aplastic AnemiaBone Marrow Failure Syndrome

Treatments studied

Part of Blood & lymphatic clinical trials.

This trial tests a “half-matched” stem cell transplant for children and teens with severe aplastic anemia when a fully matched donor isn’t available. It may help rebuild blood-making cells after prior treatments did not work well enough.

Summary written for real people, not researchers, by Clin2.

Phase
Phase 2
Enrollment
21 people
Ages
Up to 21 years
Study type
Interventional

Who can take part

  • Be age 21 or younger when you enroll
  • Have severe aplastic anemia or a single blood cell type that’s very low, based on blood tests and bone marrow findings
  • No well-matched sibling or fully matched unrelated donor available in time
  • Have either failed immune-suppressing treatment or your disease returned after stopping it (unless your case is extremely unlikely to respond)
  • Have a family donor who is half-matched (at least 3 of 6 genetic matches)
  • Meet heart, kidney, lung, liver health, and general activity strength requirements

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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