Long-term study of muscular dystrophy functions
Part of Bones, joints & muscles, Brain & nervous system, Eyes & vision, Genetic & congenital, Heart & circulation, Lungs & breathing clinical trials.
This study tracks changes in muscle strength and breathing over time in people with certain types of muscular dystrophy. It helps researchers develop better tests to measure how the disease progresses.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You are between 6 and 50 years old
- You have muscle weakness in your shoulders, hips, or trunk that started in childhood or adulthood
- You have a genetic diagnosis of limb-girdle muscular dystrophy (LGMD), myotonic dystrophy type 2 (DM2), or late-onset Pompe disease (LOPD)
- Your breathing test (FVC) shows at least 30% of expected function
- You do not have another medical condition that would make testing unsafe or confusing
- You are not currently taking an experimental drug in another clinical trial
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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