Study of disease progression in women with X-linked adrenoleukodystrophy
Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism clinical trials.
This study follows women with a genetic condition called X-linked adrenoleukodystrophy (ALD) over time to see how the disease progresses. It includes annual check-ups and MRI scans of the brain and spinal cord to monitor changes.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You must be a woman aged 18 or older.
- You must have X-linked ALD confirmed by a genetic test, abnormal very long-chain fatty acid levels, or a family history of the condition.
- You must be willing to attend yearly visits that include brain and spinal cord MRI scans.
- You cannot have been treated with the drug leriglitazone in the past or currently.
- You cannot be pregnant or breastfeeding.
- You must be covered by French social security or a similar health system.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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