Clin2
NCT06789913Possibly a fitRecruiting

Testing RLY-2608 for growth disorders linked to PIK3CA mutations

PIK3CA-Related Overgrowth Spectrum (PROS)Lymphatic MalformationsVascular MalformationsPIK3CA MutationCLOVES SyndromeKlippel Trenaunay SyndromeMegalencephaly-capillary Malformation Polymicrogyria Syndrome (MCAP)Vascular Anomalies

Treatments studied

Part of Blood & lymphatic, Genetic & congenital, Heart & circulation clinical trials.

This trial tests a new medicine, RLY-2608, that targets the specific genetic change (PIK3CA mutation) causing overgrowth conditions. It aims to see if the drug can slow or stop the growth of affected tissues.

Summary written for real people, not researchers, by Clin2.

Phase
Phase 2
Enrollment
277 people
Ages
2 years and older
Study type
Interventional

Who can take part

  • You must have a condition called PROS or another overgrowth condition linked to PIK3CA mutation
  • A PIK3CA mutation must be found in tissue from your overgrowth or in your blood
  • You should be able to do most daily activities on your own (performance status score of at least 50)
  • You must agree to provide a sample of the affected tissue or fluid, or allow a biopsy if it's safe
  • You cannot have had any other treatment for your condition within a certain time before starting the study

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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