Enzyme therapy study for Fabry disease patients
Part of Brain & nervous system, Genetic & congenital, Heart & circulation, Hormones & metabolism clinical trials.
This trial tests if enzyme replacement therapy works well and is safe for Fabry disease. It is for people who are already prescribed this treatment.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You have been diagnosed with Fabry disease
- You are between 8 and 65 years old
- You have been prescribed a course of enzyme replacement therapy (Fabagal, Fabrazyme, Replagal)
- You are not on dialysis or have not had a kidney transplant
- You are not pregnant or breastfeeding
- You and/or your legal representative agree to join the study and share your data
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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