Romiplostim for children and young adults with severe aplastic anemia
Treatments studied
Part of Blood & lymphatic clinical trials.
This study tests a medication called romiplostim, which helps the body make more blood cells, for children and young adults with severe aplastic anemia. It may help improve blood counts and reduce the need for transfusions.
Summary written for real people, not researchers, by Clin2.
Who can take part
- Must be between 2 and 21 years old.
- Have a confirmed diagnosis of severe aplastic anemia (newly diagnosed, or that has returned or not improved after treatment).
- Must be under the care of a pediatric blood specialist.
- May need to be willing to delay a stem cell transplant if a donor is available — at least for 12 weeks.
- Must agree to use contraception if able to become pregnant.
- Cannot currently be taking other similar blood cell–boosting drugs (like Promacta) or androgens.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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