RNA drug study for prion disease safety
Part of Brain & nervous system, Genetic & congenital, Infections, Mental health clinical trials.
This study tests an RNA-based drug designed to turn off the gene that causes prion disease. It aims to see if the drug is safe in people with early-stage symptoms.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You have symptoms of prion disease that affect your daily life.
- You have been diagnosed with probable prion disease using standard criteria.
- A lab test (either spinal fluid or genetic) confirmed prion disease.
- Your disease is not too advanced — you should be able to do daily activities with some help.
- You have a friend or family member who can come with you to visits.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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