Long-term vatiquinone study for Friedreich's ataxia
Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism clinical trials.
This study tests a drug called vatiquinone to see if it can help slow the progression of Friedreich's ataxia over the long term. You may be able to join if you are at a certain stage of the disease and are still able to walk.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You have a confirmed diagnosis of Friedreich's ataxia caused by a specific genetic change (GAA repeat expansion) in both genes.
- Your motor function is mild to moderate, and you can still walk (with or without assistance).
- Your symptoms have been stable in the weeks before the study starts.
- You are willing to avoid certain foods, supplements, and medicines (like grapefruit juice, St. John's wort, and some drugs) for at least 4 weeks before and during the study.
- You have not used the FA drug omaveloxolone recently, or if you did, you stopped long enough.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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