Clin2
NCT05813678Possibly a fitRecruiting

Long-term safety monitoring for Palynziq in PKU

Phenylketonuria (PKU)

Treatments studied

Part of Brain & nervous system, Genetic & congenital, Hormones & metabolism clinical trials.

This study tracks the long-term safety of Palynziq (pegvaliase) in people with PKU as they take the medicine over time. It may help you and other patients understand long-term side effects and whether Palynziq stays safe.

Summary written for real people, not researchers, by Clin2.

Phase
N/A
Enrollment
450 people
Ages
Any age
Study type
Observational

Who can take part

  • You have a confirmed diagnosis of PKU based on your local medical standard.
  • You are currently taking Palynziq (pegvaliase) or will start within 30 days after joining.
  • You (or your legally authorized representative) can sign a consent form after the study is explained.
  • You are not able to join if you are currently in another medicine/device/procedure study.
  • You have not already been enrolled in this same PALace study before.

View the official record on ClinicalTrials.gov

Quick eligibility check

Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.

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