Oral study treatment for mitochondrial disease symptoms
Part of Bones, joints & muscles, Brain & nervous system, Ear, nose & throat, Eyes & vision, Genetic & congenital, Heart & circulation, Hormones & metabolism, Mental health clinical trials.
This study tests an oral medication (glycerol tributyrate) in people with certain mitochondrial diseases. It aims to see if the medication can help improve symptoms by supporting energy production in cells.
Summary written for real people, not researchers, by Clin2.
Who can take part
- You must be between 18 and 65 years old.
- You need a confirmed genetic diagnosis of MELAS or LHON-Plus with a specific gene change.
- You must have symptoms like muscle weakness, exercise intolerance, or nerve problems.
- You must be able to swallow capsules and give written consent.
- You cannot be pregnant, breastfeeding, or currently in another clinical trial.
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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