Glycerol tributyrate for MELAS or LHON-Plus
Part of Bones, joints & muscles, Brain & nervous system, Ear, nose & throat, Eyes & vision, Genetic & congenital, Heart & circulation, Hormones & metabolism, Mental health clinical trials.
This trial tests a medicine called glycerol tributyrate in people with certain mitochondrial disorders (MELAS or LHON-Plus). The goal is to see if it can help with symptoms like muscle weakness, tiredness, and other issues caused by problems with the energy centers in your cells.
Summary written for real people, not researchers, by Clin2.
Who can take part
- Be 18 to 65 years old
- Have a confirmed diagnosis of MELAS or LHON-Plus with certain genetic changes
- Have symptoms like muscle weakness or exercise intolerance
- Not be pregnant or breastfeeding, and use birth control if sexually active
- Be able to swallow capsules and travel to the study site
Quick eligibility check
Answer a few plain-language questions, based on this study's own requirements, to get a preliminary sense of fit.
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